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babarasmith

Rare Disease Diagnostic Development to Small Molecule Drug Development

Rare Disease Diagnostic Development to Small Molecule Drug Development

Rare diseases, also known as orphan diseases, affect a small percentage of the population, making them particularly challenging to diagnose and treat. However, thanks to advancements in medical research and technology, significant progress has been made in the field of rare disease drug development, from developing accurate diagnostic tools to making effective small-molecule drugs.  …

Disease Model Development to Enhance Preclinical Rare Disease Research

Disease Model Development to Enhance Preclinical Rare Disease Research

Rare diseases, which affect a small percentage of the population, pose unique challenges for researchers due to their limited understanding and lack of available treatment options. Rare disease models are utilized to recreate the pathophysiological processes and symptoms of rare diseases in a laboratory setting. These models offer researchers a controlled environment to investigate the…